Our genomes are filled with errors that were once impossible to correct. But in CRISPR, we finally found an extraordinarily ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...

Scribe projected to enter the clinic in mid-2026 with STX-1150, a PCSK9-targeting CRISPR epigenetic silencing therapy for durable LDL-C reduction ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in ...

Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.

Researchers have unveiled a way to flip genes back on without slicing into the genome, a shift that could make CRISPR far ...

CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...

Picture CRISPR-Cas9, a gene editing technology, as a GPS-guided scalpel: gRNA directs the Cas9 enzyme, a protein that cuts ...

A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

Innovative research into the gene-editing tool targets influenza’s ability to replicate—stopping it in its tracks.

The study used large-scale CRISPR gene-editing technology to systematically determine which genes are required as embryonic ...